Global Pompe Disease Market 2015 - Market Size, Share, Growth & Opportunities

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Global Pompe Disease Market 2015-2019 Analysis,
Growth, Industry Overview, Global Share, Size,
Trends Opportunities and Forecast 2015 - 2019
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DESCRIPTION
About Pompe Disease Pompe disease is a type of
LSD. LSD refers to a group of diseases arising
from the accumulation of specific substrates.
LSDs are progressive and have variable age of
onset and clinical symptoms. LSDs are inherited
autosomal recessive disorders. Pompe disease has
two broad sub-types infantile-onset Pompe
disease and adult-onset Pompe disease. Pompe
disease occurs as a result of mutations in the
GAA gene. These mutations are responsible for the
preventing the action of the enzyme acid
alpha-glucosidase, which is responsible for
catabolizing glycogen, thereby allowing sugar to
accumulate and reach toxic levels in the
lysosomes of cells. The buildup of glycogen in
certain organs and tissues, mostly in the
muscles, hinders the normal functions of organs.
Pompe disease is an autosomal recessive
disease.This implies that both the parents pass
on one abnormally mutated copy of the gene to
their child. A parent carrying an abnormal copy
of the gene is known as a carrier. Pompe disease
affects both men and women, irrespective of the
gender. Pompe disease affects people across all
ethnicities and races. Individuals affected with
Pompe disease acquire the disease at birth,
however, the onset of symptoms varies
extensively. The Global Pompe Disease market to
grow at a CAGR of 11.79 percent over the period
2014-2019.   Read more details athttp//www.bigma
rketresearch.com/global-pompe-disease-2015-2019-ma
rket
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REPORT OVERVIEW
Covered in this Report Global Pompe Disease
Market report covers the present scenario and the
growth prospects of the Global Pompe Disease
market for the period 2015-2019. To calculate the
market size, the report considers revenue from
the sales of drugs available in the market for
the management of Pompe disease.   The report
also presents the vendor landscape and a
corresponding detailed analysis of the major
vendors in the Global Pompe Disease market. The
report also considers the revenue that is likely
to be generated from the drug candidates that are
under various phases of development. In addition,
it discusses the major drivers that influence the
growth of the market, the challenges faced by the
vendors and the market at large, as well as the
key trends that contribute to the growth the
market.   Global Pompe Disease Market
2015-2019, has been prepared based on an in-depth
market analysis with inputs from industry
experts. The report covers the Americas, and the
EMEA and APAC regions it also covers the Global
Pompe Disease market landscape and its growth
prospects over the coming years. The report also
includes a discussion of the key vendors
operating in this market.  
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KEY BENEFITS
Key Regions Americas APAC EMEA   Key
Vendors Amicus Therapeutics BioMarin
Pharmaceutical Genzyme   Other Prominent
Vendors Audentes Therapeutics EpiVax
Oxyrane Sangamo BioSciences Valerion
Therapeutics
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KEY AUDIENCES
Market Driver Special Provisions for Orphan
Drugs For a full, detailed list, view our
report   Market Challenge Limited Patient
Population For a full, detailed list, view our
report   Market Trend Regulatory Assistance in
Emerging Nations For a full, detailed list,
view our report  
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KEY AUDIENCES
Key Questions Answered in this Report What will
the market size be in 2019 and what will the
growth rate be? What are the key market
trends? What is driving this market? What are
the challenges to market growth? Who are the
key vendors in this market space? What are the
market opportunities and threats faced by the key
vendors? What are the strengths and weaknesses
of the key vendors?   Enquire about report
http//www.bigmarketresearch.com/report-enquiry/22
1060
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Get Full Information At
http//www.bigmarketresearch.com/global-pompe-dise
ase-2015-2019-market