Pompe Disease Market Trends, Forecast 2030

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Pompe Disease Market Size Worth USD 1,971.13
Million in 2030
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Increasing prevalence of Pompe Disease is one of
the key factors driving Pompe Disease market
revenue growth
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Our Model
Market Analysis
Financial Analysis
Distribution Channel Analysis
Brand Analysis
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Competitor Analysis
Product Analysis
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Demand Analysis
Risk Analysis
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Business Plan Parameters
End Use Analysis
Demand Availability Analytics
Market Entry Strategy
Restructuring Revival
New Product Strategy
Product Planning / Strategy
SWOT Analysis
Marketing / Distribution Channel Feasibility
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Customer Identification Survey
Competitive Landscape / MA Feasibility
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Market Summary
The global Pompe Disease market size reached USD
1,386.09 Million in 2021 and is expected to
register a revenue CAGR of 3.9 during the
forecast period, according to a latest analysis
by Emergen Research. Increasing prevalence of
Pompe Disease, rising number of clinical studies
and trials in the field of Pompe-disease-based
treatments, and introduction of novel and
advanced screening platforms for early diagnosis
are crucial factors driving market revenue
growth. Pompe disease is a hereditary,
frequently fatal ailment that affects the heart
and skeletal muscles. It is thought to affect one
in every 40,000 births, according to the National
Institute of Neurological Disorders and Stroke.
Mutations in a gene that produces an enzyme
called acid alpha-glucosidase cause it (GAA).
Many researchers are trying to better understand
the earliest features and manifestations of
late-onset Pompe disease novel screening
platforms such as newborn screening.
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Market Summary
Some Key Highlights From the Report The
Chaperone Advanced Replacement Therapy (CHART)
segment accounted for a moderate revenue share in
2021. Chaperone therapy for Pompe disease entails
the use of small compounds that bind to the
defective GAA enzyme, assisting it in assembling
correctly and restoring normal enzyme activities.
The use of chaperone therapy as an alternative
treatment for Pompe's illness is being
investigated. It employs small-molecule ligands
that attach directly to the faulty enzyme,
allowing it to fold in the most stable
conformation possible. Many companies are
actively assessing and analyzing the clinical
efficacy of this therapy, which is undergoing
clinical development. For instance, Amicus
Therapeutics application for AT-GAA to be
licensed as a therapeutic for late-onset Pompe
illness is now being evaluated by the U.S.  The
hospitals segment accounted for a significant
revenue share in 2021. Many hospitals are working
on novel and improved ways to facilitate in the
early detection of Pompe disease, with the goal
of quickly transferring patients with mild
symptoms to expert centers. Patients would be
able to be properly tested and diagnosed,
allowing them to begin treatment as soon as
possible. The market in Europe accounted for a
moderate revenue share in 2021. This is
attributed to increased funding and partnerships
between major companies to conduct clinical
studies on the effectiveness of novel therapeutic
options for the treatment of Pompe disease is
another factor, which is expected to
significantly contribute to revenue growth of the
region. 
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Market Summary
Some Key Highlights From the Report Key players
in the global market include Sanofi S.A., Amicus
Therapeutics, Inc., BioMarin Pharmaceutical,
Valerion Therapeutics, Oxyrane, Genzyme
Corporation, EpiVax, Inc., Bayer AG, Audentes
Therapeutics, and Sangamo Therapeutics Request
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Market Summary
Emergen Research has segmented global Pompe
Disease market on the basis of type, treatment
type, end-use and region Type Outlook (Revenue,
USD Million 2019-2030) Infantile-Onset Pompe
Disease (IOPD) Late-Onset Pompe Disease
(LOPD) Treatment Type Outlook (Revenue, USD
Million 2019-2030) Enzyme Replacement Therapy
(ERT) Chaperone Therapy Substrate Replacement
Therapy (SRT) Others End-Use Outlook (Revenue,
USD Million 2019-2030) Hospitals Diagnostic
Centers Others Read More_at_ https//www.emergenrese
arch.com/industry-report/pompe-disease-market
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Parameter Details
Market Size Estimation Period 2022-2030
Base Year Considered 2021
Historical Data 2019-2020
Forecast Period 2022-2030
Quantitative Units Revenue in USD million CAGR from 2020 to 2028
Segments Covered Types, Application, End-Users, Regions more.
Countries Included The U.S., Germany, U.K., Italy, China, India, Japan, Brazil
Report Coverage Revenue Forecast, Company Ranking, Competitive Landscape, Growth Factors, and Trends
Regions Scope North America, Europe, Asia Pacific, Latin America, Middle East and Africa
Customization Scope 10 hours of free customization expert consultation
Pricing and Purchase Options Explore Different Purchase Options Request for Discount to Avail New Year Discount
MARKET SEGMENTATION
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Regional Share Dynamics
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